Fact Sheets, Rare Diseases Cell and Gene Therapy Manufacturing at Evotec Modena 14 November 2022 Learn more
Metabolic Disease & Complications, Posters, Rare Diseases Automated Utrophin Imaging for Duchenne Muscular Dystrophy 11 March 2021 Learn more
Metabolic Disease & Complications, Posters, Rare Diseases Novel Small Molecule Treatment Options for FSHD 11 March 2021 Learn more
Articles & Whitepapers, Hit & Target ID/Validation, Metabolic Disease & Complications, Proteomics, Metabolomics & Biomarkers, Rare Diseases AhR as a Molecular Target of the Utrophin Modulator Ezutromid 11 March 2021 Learn more
Articles & Whitepapers, Biologics, Proteomics, Metabolomics & Biomarkers, Rare Diseases A Multidisciplinary Approach to Gene Therapy Development 11 March 2021 Learn more
Articles & Whitepapers, Rare Diseases Orphan Drugs: Overcoming the Development Challenges 2 March 2021 Learn more
Rare Diseases, Videos & Webinars Webinar: Overcoming CMC challenges in Rare Disease Drug Development 18 February 2021 Learn more
Biologics, Rare Diseases, Videos & Webinars Joint Webinar: Novel Gene Therapies for Rare Diseases 18 February 2021 Learn more